Craig McDonald, M.D.

University of California at Davis (USA)

Pat Furlong

Parent Project Muscular Dystrophy (USA)

Michelle Eagle, Ph.D., M.Sc., MCSP

Atom International Ltd (UK)

Timothy Franson, M.D., FACP, FIDSA

Faegre Drinker Biddle & Realth LLP (USA)

Michael Taylor, M.D., Ph.D.

Texas Children’s Hospital (USA)

Eugenio Mercuri, M.D.

Catholic University of the Sacred Heart (Italy)

Chet Villa, M.D.

Cincinnati Children’s Hospital Medical Center (USA)

Jonathan Soslow, M.D., MSCI

Vanderbilt University Medical Center (USA)

Kan Hor, M.D.

Nationwide Children’s Hospital (USA)