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Publications

Our Science

Our Science

  • Deramiocel (Biologic Medicine)
  • Exosomes Technology
  • Publications
  • Strategic Partnerships

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PPMD 2026 (HOPE-3)

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PPMD 2026 (Late-Breaking HOPE-2 OLE 5-Year Results)

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American Society of Gene & Cell Therapy (ASGCT) 2026 Annual Meeting Presentation

Jonathan H. Soslow, Chet Villa, Russell J Butterfield, Michael Binks, Kati Maharry, Nathan Horgan, Kristi Elliott, Minghao Sun, Mark Awadalla, Linda Marban, Craig McDonald

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Extracellular Vesicles Delivered a Functional ARG1 Enzyme and Restored Its Activity in a Mouse Model of ARG1-D Resulting in Improved Lifespan

Li-En Hsieh, Mafalda Cacciottolo, Michael J. LeClaire, William Morrison, Bailey Murphy, Christy Lau, Kristi Elliott, Linda Marban and Minghao Sun

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American Academy of Neurology (AAN) 2026 Presentation

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2026 MDA Conference Presentation

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StealthX: A Versatile and Potent Exosome-Based Vaccine Platform for the Next Pandemic

Minghao Sun, Kristi Elliott

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A Systematic Framework for the Scalable Loading of Therapeutic siRNA and PMO into Exosomes

Firouz Mohsenian, Meena Murali, David Tran, Daniel Leychkis, William Morrison, Kristi Elliott, Minghao Sun

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A Novel In Vitro Potency Assay Demonstrating the Anti-Fibrotic Mechanism of Action of CDCs in Deramiocel

Yujia Li, Justin B. Nice, Marya Kozinova , Stephanie Adachi, Linda Marban, Kristi Elliott and Minghao Sun

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Multivalent Exosome Based Protein Vaccine: A “Mix and Match” Approach to Epidemic Viruses’ Challenges

Mafalda Cacciottolo, Li-En Hsieh, Yujia Li, Michael J. LeClaire, Ciana L. Mora, Christy Lau, Charles Dwyer, Kristi Elliott and Minghao Sun

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